Senior Scientist, mRNA Design & Platform Innovation
Core
Design and optimize mRNA architectures and RNA components for Prime Editing systems to enable gene editing therapies.
Role type
Senior Scientist, mRNA Design & Platform Innovation
Builds
Novel mRNA architectures and Prime Editing platform technologies for gene editing therapies
Domain
Biotechnology / Gene Editing / RNA Biology
Deliverable
production ML models | product features | dashboards & analysis | research | client delivery | infrastructure | physical/clinical work
Required skills
mRNA biology and engineering, in vitro transcription (IVT), UTR design and optimization, codon usage, RNA secondary structure analysis, experimental design, data interpretation, scientific communication, laboratory safety compliance, mentoring research associates
Preferred skills
Next-generation RNA formats (circular RNA, modified nucleosides), CRISPR-based gene editing technologies, computational tools for mRNA design, in vivo animal model translation, non-viral/viral delivery systems (LNP/AAV), human biology knowledge
Technologies
Prime Editing platform, IVT systems, LNP, AAV
Responsibilities
Design and construct novel mRNA architectures for Prime Editing applications; execute experiments to probe structure-function relationships; lead discovery efforts for novel therapeutic approaches; partner with cross-functional teams to translate platform advances; maintain engagement with scientific literature; communicate research findings; mentor research associates and interns
Seniority
Senior, hands-on IC with mentorship responsibilities