Scientist, Target Discovery & Validation
Core
Identify novel drug targets in various indications and tissues, and lead preclinical proof of concept studies to validate target feasibility.
Role type
Scientist, Target Discovery & Validation
Builds
Drug candidates from idea to clinic
Domain
Biopharmaceuticals / RNA therapeutics / Human genetics
Deliverable
production ML models | product features | dashboards & analysis | research | client delivery | infrastructure | physical/clinical work
Required skills
Mammalian disease models, human genetics, assay development, project management, CRO management, mentoring
Preferred skills
Postdoc experience, disease biology focus, publication record, human genetics for mechanism
Technologies
Animal models, in vitro disease models, genomic approaches
Responsibilities
Identify promising novel targets with genetics/omics/clinical teams; Design and execute proof of concept experiments in animal and in vitro models; Design studies, coordinate activities, and lead from the bench; Oversee lead discovery activities for drug candidate selection; Develop assays to monitor target engagement/pharmacodynamic responses; Manage relationships with CROs and academic collaborators; Mentor junior scientists.
Seniority
Mid-level Scientist (PhD + 0-2 years)