Regional Medical Lead, Rare Diseases SMA
Core
Strategic medical leadership for Rare Diseases (SMA) portfolio, connecting global strategy with regional affiliate needs to drive pipeline development, launch readiness, and evidence generation.
Role type
Senior Medical Affairs Leader (Management)
Builds
Regional medical strategies, evidence generation plans, and launch readiness activities for SMA assets.
Domain
Biotechnology / Rare Diseases (SMA)
Required skills
Advanced scientific or medical degree (MD, PhD, PharmD), 10+ years pharma/biotech experience, Rare Diseases (SMA) expertise, Medical Affairs strategy development, cross-functional stakeholder influence, external medical expert relationship building, scientific communication.
Preferred skills
Experience at affiliate and above-market levels, navigating matrix organizations, translating regional insights to global strategy.
Responsibilities
Lead regional medical strategy and execution across the TA portfolio; Provide input to clinical development, evidence generation, and launch activities; Lead regional medical initiatives including advisory boards and scientific communications; Partner with affiliates and cross-functional teams to ensure consistent medical voice; Identify evidence and patient journey gaps; Build partnerships with external medical experts and scientific societies; Support development of regional medical plans aligned with Global/PDC priorities.
Seniority
Senior, Management level