Scientist, Neuromuscular Research
Core
Design, execute, and analyze experiments to investigate neuromuscular disease mechanisms, identify therapeutic targets, and evaluate candidate therapeutics using iPSC-derived and rodent models.
Role type
Scientist, neuromuscular research (IC)
Builds
Preclinical research data and therapeutic candidate evaluation
Domain
Biotechnology / Neuromuscular disorders
Deliverable
production ML models | product features | dashboards & analysis | research | client delivery | infrastructure | physical/clinical work
Required skills
iPSC-derived myotube and cardiomyocyte culture, in vivo muscle function assessment, biochemistry and molecular biology techniques, statistical analysis, experimental design and troubleshooting
Preferred skills
Genetic neuromuscular disorders (DMD, DM1), RNA therapies, antisense oligonucleotides, LNP
Technologies
GraphPad Prism
Responsibilities
Independently design, execute, analyze, and interpret experiments; Develop and optimize molecular and cellular assays; Characterize muscle disease phenotypes in rodent models; Present data in cross-functional forums
Seniority
Junior to Mid-level, hands-on IC