Director, Translational Medicine Expert (Neurodegeneration)
Core
Lead end-to-end translational strategy for neurodegenerative programs, bridging preclinical research to early clinical development (Phase 1–2) and ensuring competitive differentiation of neuromuscular assets.
Role type
Director, Translational Medicine Expert (Neurodegeneration)
Builds
Early clinical development programs (Phase 1/2) for neurodegenerative and neuromuscular assets
Domain
Biopharma / Neurodegeneration / Translational Medicine
Deliverable
production ML models | product features | dashboards & analysis | research | client delivery | infrastructure | physical/clinical work
Required skills
Translational medicine strategy, early clinical development design, biomarker strategy, clinical endpoint selection, trial design, cross-functional leadership, external scientific collaboration, patient-centered development
Preferred skills
Pharmaceutical/biotech industry experience, portfolio contribution, business development input
Technologies
Imaging platforms, omics platforms, decentralized trial models
Responsibilities
Define and execute integrated translational strategies across neurodegeneration programs; Lead translational components from preclinical to Phase 1/2 clinical studies; Drive program progression through key decision gates (e.g., IND, TDP, IDPA); Collaborate on development and validation of molecular biomarkers and functional endpoints; Co-lead design and execution of early clinical studies including dose escalation strategies; Serve as core Translational Medicine representative within global project teams; Build and lead collaborations with academic KOLs and patient advocacy groups; Integrate patient voice into translational and clinical strategies
Seniority
Director, strategic leadership & hands-on execution