Director, Medical Affairs - Rare Diseases
Core
Lead medical strategy and scientific engagement for investigational and approved therapies in rare diseases across Europe.
Role type
Director, Medical Affairs (Rare Diseases)
Builds
Medical strategies, scientific partnerships, and evidence generation for rare disease assets.
Domain
Biopharmaceuticals, Rare Diseases, Genetic Medicine
Required skills
Medical strategy leadership, scientific partnership development, evidence generation, drug lifecycle management, budget and timeline management, compliance adherence
Preferred skills
Rare genetic diseases expertise, gene therapy knowledge, regenerative medicine experience, product launch leadership, multi-country management
Technologies
None stated
Responsibilities
Lead medical strategies and tactical plans across assigned rare disease assets; Provide scientific and medical leadership throughout pre-launch, launch and post-launch phases; Establish scientific partnerships with healthcare professionals, researchers, advocacy organisations, payers and other external stakeholders; Drive evidence generation through Medical Affairs studies, data analysis, publications and scientific communication plans; Translate clinical and country insights into recommendations supporting medical strategy, patient access and value demonstration; Manage complex priorities, budgets and timelines while maintaining scientific integrity and compliance
Seniority
Director, strategic leadership with hands-on execution
