Associate Director, Biomarker Science
Core
Oversees clinical and non-clinical biomarker development for Sarepta's siRNA pipeline, focusing on early and translational programs in rare diseases like Duchenne muscular dystrophy.
Role type
Associate Director, Biomarker Science (Translational Biology)
Builds
siRNA therapeutics for muscle, central nervous system, and cardiac diseases
Domain
Biopharmaceuticals / Rare Diseases / Neurobiology / siRNA
Deliverable
production ML models | product features | dashboards & analysis | research | client delivery | infrastructure | physical/clinical work
Required skills
biomarker discovery and development, siRNA therapeutics expertise, neurobiology/neuromuscular biology, bioassay development and validation, -omics platforms (RNASeq, Single cell, proteomics), regulatory document authoring, vendor management, cross-functional collaboration
Preferred skills
experience in outward-facing roles, managing multiple complex projects simultaneously
Technologies
RNASeq, Single cell, proteomics, protein-binding assay platforms
Responsibilities
Develop and implement biomarker strategies for nonclinical, translational, and clinical programs; conduct literature reviews to identify novel PK or PD biomarkers; perform data analysis to interpret non-clinical and clinical PD data; oversee Contract Research Organizations for assay development and validation; represent Translational Biology on internal sub-teams; participate in regulatory writing for INDs, CTAs, and NDAs
Seniority
Senior, hands-on IC with strategic oversight