Medical Director, US Medical Affairs – Rare Diseases (Friedreich's Ataxia)
Core
US Medical Lead for Friedreich's Ataxia, accountable for developing and executing the integrated US Medical Affairs strategy, including lifecycle expansion and evidence generation.
Role type
Senior IC medical director (rare diseases)
Builds
US medical strategy, evidence generation plans, and medical education initiatives for Friedreich's Ataxia therapies
Domain
Biotechnology / Rare Diseases / Neurodegenerative Disorders
Required skills
strategic planning, evidence generation, stakeholder engagement, scientific communication, budget management, cross-functional leadership
Preferred skills
Friedreich's Ataxia expertise, launch execution, indication expansion, patient advocacy partnership, global collaboration
Technologies
none stated
Responsibilities
Lead annual and long-range medical planning; drive medical readiness for lifecycle expansion; lead US evidence generation strategy; establish relationships with key opinion leaders and advocacy organizations; develop scientific communications and medical education initiatives; mentor colleagues across Medical Affairs
Seniority
Senior, hands-on IC