CareerPlan

Medical Director, US Medical Affairs – Rare Diseases (Friedreich's Ataxia)

Cambridge, MA, USFull-time$225k–$310k2026-10-20 → 2026-11-12
Based in United States

Core

US Medical Lead for Friedreich's Ataxia, accountable for developing and executing the integrated US Medical Affairs strategy, including lifecycle expansion and evidence generation.

Role type

Senior IC medical director (rare diseases)

Builds

US medical strategy, evidence generation plans, and medical education initiatives for Friedreich's Ataxia therapies

Domain

Biotechnology / Rare Diseases / Neurodegenerative Disorders

Required skills

strategic planning, evidence generation, stakeholder engagement, scientific communication, budget management, cross-functional leadership

Preferred skills

Friedreich's Ataxia expertise, launch execution, indication expansion, patient advocacy partnership, global collaboration

Technologies

none stated

Responsibilities

Lead annual and long-range medical planning; drive medical readiness for lifecycle expansion; lead US evidence generation strategy; establish relationships with key opinion leaders and advocacy organizations; develop scientific communications and medical education initiatives; mentor colleagues across Medical Affairs

Seniority

Senior, hands-on IC