Senior Study Director, Rare Disease Translational Center
Core
Leading and overseeing complex scientific studies to build clinically relevant mouse and cell-based models for treating rare diseases using gene therapy and RNA-based treatments.
Role type
Senior Study Director (Research & Development)
Builds
Custom mouse and cell-based/in vitro models with clinical mutations
Domain
Biotechnology / Rare Disease Research / Preclinical Research
Required skills
Strategic planning, regulatory compliance (GLP, ICH), team leadership, data analysis, statistical analysis, risk mitigation, protocol development
Preferred skills
Advanced knowledge of genetic and molecular techniques, experience in pharmaceutical/biotech/CRO environments
Technologies
SAS, R, SPSS
Responsibilities
Develop strategic plans for scientific studies, lead study execution and reporting, provide scientific guidance, ensure regulatory compliance, mentor multidisciplinary teams, oversee data analysis and reporting, identify and mitigate project risks
Seniority
Senior, hands-on IC with leadership responsibilities