Senior Director, Epidemiology and Real World Evidence
Core
Enterprise expert in epidemiology and real-world evidence (RWE) supporting Medical Affairs-led scientific and clinical objectives for neuromuscular diseases.
Role type
Senior Director, Epidemiology and Real World Evidence
Builds
Evidence strategies, observational and interventional studies, safety surveillance, and regulatory documentation for DMD, DM1, FSHD, and Pompe disease.
Domain
Biopharmaceuticals / Rare Diseases / Neuromuscular Disorders
Deliverable
production ML models | product features | dashboards & analysis | research | client delivery | infrastructure | physical/clinical work
Required skills
Epidemiologic methods, observational study design, real-world data sources, safety surveillance, pharmacovigilance, regulatory documentation, cross-functional partnership, scientific communication, strategic planning, budget management, vendor management.
Preferred skills
Rare diseases experience, neuromuscular disorders expertise, post-authorization safety study leadership.
Technologies
None explicitly stated
Responsibilities
Lead design and execution of epidemiologic and observational studies; establish governance and best practices for RWE; partner with Medical Affairs and HEOR on enterprise-level strategies; support drug safety and pharmacovigilance activities; manage external partners and budgets; drive scientific dissemination through publications and presentations.
Seniority
Senior Director, enterprise-level leadership